. Salwa

Gene Therapies for Spinal Muscular Atrophy and Duchenne Muscular Dystrophy: A Pathbreaking Moment in Therapeutics

. Salwa, Safia Fathima Anver Pasha, Wafeeqa x Wafeeqa Fatima & Suresh Kumar Srinivasamurthy · Journal of Pharmaceutical Research International · 2022

Background: Gene therapy has proved to be a boon for neuromuscular diseases. A concept introduced in the early 1960’s, has been put into clinical practice in the past 5-10 years. The process by which a healthy gene replaces a defective gene in a human body through vectors is trul...